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Pediatrics Inborn Errors of Metabolism 2c8ce2cd

Which glycogen storage disease does not affect muscles?

A
Type 1
B
Type 2
C
Type 3
D
Type 4
High-Yield Explanation
a. Type 1(Ref: Nelson's 20/e p 715-725, Ghai 8/e p 655-657)Type 2 Pompe disease predominantly involves muscles, while type I GSD involves liver.Although type 2 and type 3 GSD are predominantly liver glycogenoses, skeletal muscle involvement may also be seen.

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