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Biochemistry General dbf73ad7

Enzyme replacement therapy is not available for?

A
Gaucher's disease
B
Tay sach disease
C
Pompe's disease
D
Hurler syndrome
High-Yield Explanation
Impoant diseases for which enzyme replacement therapy is available are :-Gaucher's diseaseMaroteaux Lamy syndrome (mucopolysaccharidosis VI)Hurler syndrome (mucopolysaccharidosis I)Fabry's diseaseHunter syndrome (mucopolysaccharidosis II)Pompe's disease (Type II glycogenosis)

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