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Pediatrics Disorders of Amino acid Metabolism 3274a89d

Sapropterin is used in the treatment of

A
Phenylketonuria
B
Hereditary Fructose Intolerance
C
Galactosemia
D
Gaucher's disease
High-Yield Explanation
Sapropterin, a synthetic form of tetrahydrobiopterin, which acts as a cofactor in patients with residual PAH activity, is approved by FDA to reduce phenylalanine levels in PKU. Galactosemia- Avoid milk & milk products. Hereditary Fructose Intolerance- Complete elimination of sucrose & fructose drom diet. Gaucher's disease- Enzyme replacement therapy.

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