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Biochemistry Molecular Genetics 26b2a4b1

Gene therapy is successful for the treatment of -

A
Adenosine deaminase deficiency
B
Krabbe's disease
C
Hodgkin's lymphoma
D
b thalassemia
High-Yield Explanation
Ans. is 'a' i.e., Adenosine deaminase deficiency* Gene therapy is available for:# X linked Severe Combined Immunodeficiency (SCID)# Adenosine Deaminase - SCID# Hemophilia# Chronic Lymphocytic Leukemia# Acute Lymphocytic Leukemia# Adrenoleukodystrophy# Parkinson's disease# Multiple Myeloma

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